CRISPR-mediated correction of skeletal muscle Ca2+ handling in a novel DMD patient-derived pluripotent stem cell model
Titel:
CRISPR-mediated correction of skeletal muscle Ca2+ handling in a novel DMD patient-derived pluripotent stem cell model
Auteur:
Morera, Cristina Kim, Jihee Paredes-Redondo, Amaia Nobles, Muriel Rybin, Denis Moccia, Robert Kowala, Anna Meng, Jinhong Garren, Seth Liu, Pentao Morgan, Jennifer E Muntoni, Francesco Christoforou, Nicolas Owens, Jane Tinker, Andrew Lin, Yung-Yao