Age related treatment effect in type II Spinal Muscular Atrophy pediatric patients treated with nusinersen
Titel:
Age related treatment effect in type II Spinal Muscular Atrophy pediatric patients treated with nusinersen
Auteur:
Coratti, Giorgia Pane, Marika Lucibello, Simona Pera, Maria Carmela Pasternak, Amy Montes, Jacqueline Sansone, Valeria A Duong, Tina Dunaway Young, Sally Messina, Sonia D'Amico, Adele Civitello, Matthew Glanzman, Allan M Bruno, Claudio Salmin, Francesca Tacchetti, Paola Carnicella, Sara Sframeli, Maria Antonaci, Laura Frongia, Anna Lia De Vivo, Darryl C. Darras, Basil T. Day, John Bertini, Enrico Muntoni, Francesco Finkel, Richard Mercuri, Eugenio