Randomized phase 2 trial and open-label extension of domagrozumab in Duchenne muscular dystrophy
Titel:
Randomized phase 2 trial and open-label extension of domagrozumab in Duchenne muscular dystrophy
Auteur:
Wagner, Kathryn R. Abdel-Hamid, Hoda Z. Mah, Jean K. Campbell, Craig Guglieri, Michela Muntoni, Francesco Takeshima, Yasuhiro McDonald, Craig M. Kostera-Pruszczyk, Anna Karachunski, Peter Butterfield, Russell J. Mercuri, Eugenio Fiorillo, Chiara Bertini, Enrico S. Tian, Cuixia Statland, Jeffery Sadosky, Alesia B. Purohit, Vivek S. Sherlock, Sarah P. Palmer, Jeffrey P. Binks, Michael Charnas, Lawrence Marraffino, Shannon Wong, Brenda L.