Long-term follow-up of patients with type 2 and non-ambulant type 3 spinal muscular atrophy (SMA) treated with olesoxime in the OLEOS trial
Titel:
Long-term follow-up of patients with type 2 and non-ambulant type 3 spinal muscular atrophy (SMA) treated with olesoxime in the OLEOS trial
Auteur:
Muntoni, Francesco Bertini, Enrico Comi, Giacomo Kirschner, Janbernd Lusakowska, Anna Mercuri, Eugenio Scoto, Mariacristina van der Pol, W Ludo Vuillerot, Carole Burdeska, Alexander El-Khairi, Muna Fontoura, Paulo Ives, Jane Gorni, Ksenija Reid, Carol Fuerst-Recktenwald, Sabine