Development of an academic disease registry for spinal muscular atrophy
Titel:
Development of an academic disease registry for spinal muscular atrophy
Auteur:
Mercuri, Eugenio Finkel, Richard Scoto, MariaCristina Hall, Susan Eaton, Susan Rashid, Aisha Balashkina, Julia Coratti, Giorgia Pera, Maria Carmela Samsuddin, Salma Civitello, Matthew Muntoni, Francesco