Golodirsen induces exon skipping leading to sarcolemmal dystrophin expression in patients with genetic mutations amenable to exon 53 skipping
Titel:
Golodirsen induces exon skipping leading to sarcolemmal dystrophin expression in patients with genetic mutations amenable to exon 53 skipping
Auteur:
Muntoni, F. Frank, D.E. Morgan, J. Domingos, J. Schnell, F.J. Dickson, G. Popplewell, L. Guglieri, M. Seferian, A. Monforte, M. Mercuri, E. Servais, L. Straub, V.