A multinational, randomized, double-blind, placebo-controlled Phase 2 study to assess safety and efficacy of olesoxime in Type 2 or non-ambulatory Type 3 spinal muscular atrophy
Titel:
A multinational, randomized, double-blind, placebo-controlled Phase 2 study to assess safety and efficacy of olesoxime in Type 2 or non-ambulatory Type 3 spinal muscular atrophy
Auteur:
Buchbjerg, J. Bertini, E. Dessaud, E. Mercuri, E. Muntoni, F. Kirschner, J. Reid, C. Lusakowska, A. Comi, G.P. Cuisset, J.-M. Abitbol, J.-L. Scherrer, B. Vianna, E. van der Pol, W.L. Vuillerot, C. Fontoura, P. Blaettler, T.