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Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience |
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Titel: |
Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience |
Auteur: |
Messina, Sonia Pane, Marika Sansone, Valeria Bruno, Claudio Catteruccia, Michela Vita, Giuseppe Palermo, Concetta Albamonte, Emilio Pedemonte, Marina Bertini, Enrico Binetti, Luca Mercuri, Eugenio |
Verschenen in: |
Neuromuscular disorders |
Paginering: |
Jaargang 27 (2017) nr. 12 pagina's 1084-1086 |
Jaar: |
2017 |
Inhoud: |
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Uitgever: |
Published by Elsevier B.V. |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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