Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials
Titel:
Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials
Auteur:
Mercuri, Eugenio Finkel, Richard Montes, Jacqueline Mazzone, Elena S. Sormani, Maria Pia Main, Marion Ramsey, Danielle Mayhew, Anna Glanzman, Allan M. Dunaway, Sally Salazar, Rachel Pasternak, Amy Quigley, Janet Pane, Marika Pera, Maria Carmela Scoto, Mariacristina Messina, Sonia Sframeli, Maria Vita, Gian Luca D'Amico, Adele van den Hauwe, Marleen Sivo, Serena Goemans, Nathalie Kaufmann, Petra Darras, Basil T. Bertini, Enrico Muntoni, Francesco De Vivo, Darryl C.