European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene
Titel:
European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene
Auteur:
Haas, Manuel Vlcek, Viktor Balabanov, Pavel Salmonson, Tomas Bakchine, Serge Markey, Greg Weise, Martina Schlosser-Weber, Gabriele Brohmann, Henning Yerro, Concepcion Prieto Mendizabal, Macarena Rodriguez Stoyanova-Beninska, Violeta Hillege, Hans L.