P03 Exon skipping and dystrophin restoration in Duchenne muscular dystrophy patients after systemic phosphorodiamidate morpholino oligomer treatment
Titel:
P03 Exon skipping and dystrophin restoration in Duchenne muscular dystrophy patients after systemic phosphorodiamidate morpholino oligomer treatment
Auteur:
Cirak, S. Arechavala-Gomeza, V. Guglieri, M. Feng, L. Torelli, S. Anthony, K. Garralda, M.E. Wells, D. Dickson, G. Wood, M.J.A. Wilton, S.D. Straub, V. Shrewsbury, S.B. Sewry, C. Morgan, J.E. Bushby, K. Muntoni, F.