The risks of therapeutic misconception and individual patient (n =1) “trials” in rare diseases such as Duchenne dystrophy
Titel:
The risks of therapeutic misconception and individual patient (n =1) “trials” in rare diseases such as Duchenne dystrophy
Auteur:
Aartsma-Rus, Annemieke Furlong, Pat Vroom, Elizabeth van Ommen, Gert-Jan Niks, Erik Straathof, Chiara Verschuuren, Jan Aartsma-Rus, Annemieke Ferlini, Alessandra Hagger, Lynn Heslop, Emma Karcagi, Veronika Kirschner, Jan McCormack, Pauline Moeschen, Pat Muntoni, Francesco Ouillade, Marie-Christine Rahbeck, Jes Rehmann-Sutter, Christoph Rouault, Francoise Sejersen, Tomas Vroom, Elizabeth Woods, Simon