Effect of enzyme therapy in juvenile patients with Pompe disease: A three-year open-label study
Titel:
Effect of enzyme therapy in juvenile patients with Pompe disease: A three-year open-label study
Auteur:
van Capelle, C.I. van der Beek, N.A.M.E. Hagemans, M.L.C. Arts, W.F.M. Hop, W.C.J. Lee, P. Jaeken, J. Frohn-Mulder, I.M.E. Merkus, P.J.F.M. Corzo, D. Puga, A.C. Reuser, A.J. van der Ploeg, A.T.