Pilot trial of phenylbutyrate in spinal muscular atrophy
Titel:
Pilot trial of phenylbutyrate in spinal muscular atrophy
Auteur:
Mercuri, Eugenio Bertini, Enrico Messina, Sonia Pelliccioni, Marco D'Amico, Adele Colitto, Francesca Mirabella, Massimiliano Tiziano, Francesco D Vitali, Tiziana Angelozzi, Carla Kinali, Maria Main, Marion Brahe, Christina