Cholesterol redistribution triggered by CYP46A1 gene therapy improves major hallmarks of Niemann-Pick type C disease but is not sufficient to halt neurodegeneration
Titel:
Cholesterol redistribution triggered by CYP46A1 gene therapy improves major hallmarks of Niemann-Pick type C disease but is not sufficient to halt neurodegeneration
Auteur:
Nunes, Maria João Carvalho, Andreia Neves Reis, Joana Costa, Daniela Moutinho, Miguel Mateus, Joana Mendes de Almeida, Rita Brito, Sara Risso, Daniela Nunes, Sofia Castro-Caldas, Margarida Gama, Maria João Rodrigues, Cecília M.P. Xapelli, Sara Diógenes, Maria José Cartier, Nathalie Chali, Farah Piguet, Françoise Rodrigues, Elsa
Verschenen in:
Biochimica et Biophysica Acta. Molecular basis of disease