Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-β-Cyclodextrin
Titel:
Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-β-Cyclodextrin
Auteur:
Berry-Kravis, Elizabeth Chin, Jamie Hoffmann, Anne Winston, Amy Stoner, Robin LaGorio, Lisa Friedmann, Katherine Hernandez, Mariana Ory, Daniel S. Porter, Forbes D. O'Keefe, Joan A.