Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy
Titel:
Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy
Auteur:
Mendell, Jerry R. Proud, Crystal Zaidman, Craig M. Mason, Stefanie Darton, Eddie Wang, Shufang Wandel, Christoph Murphy, Alexander P. Mercuri, Eugenio Muntoni, Francesco McDonald, Craig M.