A Phase 2 Study of AMO-02 (Tideglusib) in Congenital and Childhood-Onset Myotonic Dystrophy Type 1 (DM1)
Titel:
A Phase 2 Study of AMO-02 (Tideglusib) in Congenital and Childhood-Onset Myotonic Dystrophy Type 1 (DM1)
Auteur:
Horrigan, Joseph Gomes, Tiago Bernardino Snape, Mike Nikolenko, Nikoletta McMorn, Alison Evans, Stuart Yaroshinsky, Alex Della Pasqua, Oscar Oosterholt, Sean Lochmüller, Hanns