Intracerebroventricular Cerliponase Alfa for Neuronal Ceroid Lipofuscinosis Type 2 Disease: Clinical Practice Considerations From US Clinics
Titel:
Intracerebroventricular Cerliponase Alfa for Neuronal Ceroid Lipofuscinosis Type 2 Disease: Clinical Practice Considerations From US Clinics
Auteur:
de los Reyes, Emily Lehwald, Lenora Augustine, Erika F. Berry-Kravis, Elizabeth Butler, Karen Cormier, Natalie Demarest, Scott Lu, Sam Madden, Jacqueline Olaya, Joffre See, Susan Vierhile, Amy Wheless, James W. Yang, Amy Cohen-Pfeffer, Jessica Chu, Dorna Leal-Pardinas, Fernanda Wang, Raymond Y.