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Later efficacy of nusinersen treatment in adult patients with spinal muscular atrophy: A retrospective case study with a median 4-year follow-up |
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Titel: |
Later efficacy of nusinersen treatment in adult patients with spinal muscular atrophy: A retrospective case study with a median 4-year follow-up |
Auteur: |
Funato, Michinori Kino, Atsunari Iwata, Reina Yumioka, Misaki Yamashita, Kohei Urui, Chika Uno, Ryoya Kondo, Emi Morioka, Etsuko Ogawa, Yoko Kawamura, Akihisa Kusukawa, Toshifumi Minatsu, Hiroshi |
Verschenen in: |
Brain & development |
Paginering: |
Jaargang 46 () nr. 1 pagina's 62-67 |
Jaar: |
2024 |
Inhoud: |
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Uitgever: |
The Japanese Society of Child Neurology |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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