Helper-dependent canine adenovirus vector-mediated transgene expression in a neurodegenerative lysosomal storage disorder
Titel:
Helper-dependent canine adenovirus vector-mediated transgene expression in a neurodegenerative lysosomal storage disorder
Auteur:
Lau, Adeline A. Rozaklis, Tina Ibanes, Sandy Luck, Amanda J. Beard, Helen Hassiotis, Sofia Mazouni, Khalil Hopwood, John J. Kremer, Eric J. Hemsley, Kim M.