Efficacy and safety of selumetinib in adults with neurofibromatosis type 1 and symptomatic, inoperable plexiform neurofibromas (KOMET): a multicentre, international, randomised, placebo-controlled, parallel, double-blind, phase 3 study
Titel:
Efficacy and safety of selumetinib in adults with neurofibromatosis type 1 and symptomatic, inoperable plexiform neurofibromas (KOMET): a multicentre, international, randomised, placebo-controlled, parallel, double-blind, phase 3 study
Auteur:
Chen, Alice P Coyne, Geraldine O'Sullivan Wolters, Pamela L Martin, Staci Farschtschi, Said Blanco, Ignacio Chen, Zhongping Darrigo Jr, Luiz Guilherme Eoli, Marica Whittle, James R Nishida, Yoshihiro Lamarca, Rosa de la Rosa Rodriguez, Randolph Adeyemi, Ayo Herrero, Idoia Llorente, Nereida Diede, Scott J Dombi, Eva Wolkenstein, Pierre