Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series
Titel:
Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series
Auteur:
Shneider, Neil A Harms, Matthew B Korobeynikov, Vlad A Rifai, Olivia M Hoover, Benjamin N Harrington, Elizabeth A Aziz-Zaman, Sonya Singleton, Jessica Jamil, Arish Madan, Vikram R Yasek, Julia Lee, Ikjae Andrews, Jinsy A Smiley, Richard M Alam, Mahabub M Black, Lauren E Shin, Minwook Watts, Jonathan K Walk, David Newman, Daniel Pascuzzi, Robert M Weber, Markus Neuwirth, Christoph Da Cruz, Sandrine Soriano, Armand Lane, Roger Henry, Scott Mathews, Joel Jafar-Nejad, Paymaan Norris, Dan Rigo, Frank Brown, Robert H Miller, Stephan Crean, Rebecca Bennett, C Frank