Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial
Titel:
Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial
Auteur:
McDonald, Craig M Marbán, Eduardo Hendrix, Suzanne Hogan, Nathaniel Ruckdeschel Smith, Rachel Eagle, Michelle Finkel, Richard S Tian, Cuixia Janas, Joanne Harmelink, Matthew M Varadhachary, Arun S Taylor, Michael D Hor, Kan N Mayer, Oscar H Henricson, Erik K Furlong, Pat Ascheim, Deborah D Rogy, Siegfried Williams, Paula Marbán, Linda