Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Titel:
Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Auteur:
McDonald, Craig M Campbell, Craig Torricelli, Ricardo Erazo Finkel, Richard S Flanigan, Kevin M Goemans, Nathalie Heydemann, Peter Kaminska, Anna Kirschner, Janbernd Muntoni, Francesco Osorio, Andrés Nascimento Schara, Ulrike Sejersen, Thomas Shieh, Perry B Sweeney, H Lee Topaloglu, Haluk Tulinius, Már Vilchez, Juan J Voit, Thomas Wong, Brenda Elfring, Gary Kroger, Hans Luo, Xiaohui McIntosh, Joseph Ong, Tuyen Riebling, Peter Souza, Marcio Spiegel, Robert J Peltz, Stuart W Mercuri, Eugenio