Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations: a prospective phase II trial
Titel:
Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations: a prospective phase II trial
Auteur:
Kerem, Eitan Hirawat, Samit Armoni, Shoshana Yaakov, Yasmin Shoseyov, David Cohen, Michael Nissim-Rafinia, Malka Blau, Hannah Rivlin, Joseph Aviram, Micha Elfring, Gary L Northcutt, Valerie J Miller, Langdon L Kerem, Batsheva Wilschanski, Michael