Multiple isogenic GNE-myopathy modeling with mutation specific phenotypes from human pluripotent stem cells by base editors
Title:
Multiple isogenic GNE-myopathy modeling with mutation specific phenotypes from human pluripotent stem cells by base editors
Author:
Park, Ju-Chan Kim, Jumee Jang, Hyun-Ki Lee, Seung-Yeon Kim, Keun-Tae Kwon, Eun-Ji Park, Seokwoo Lee, Hyun Sik Choi, Hyewon Park, Seung-Yeol Choi, Hee-Jung Park, Soon-Jung Moon, Sung-Hwan Bae, Sangsu Cha, Hyuk-Jin