PLGA-Nanoparticles for Intracellular Delivery of the CRISPR-Complex to Elevate Fetal Globin Expression in Erythroid Cells
Titel:
PLGA-Nanoparticles for Intracellular Delivery of the CRISPR-Complex to Elevate Fetal Globin Expression in Erythroid Cells
Auteur:
Cruz, Luis J. van Dijk, Thamar Vepris, Olena Li, Tracy M.W.Y. Schomann, Timo Baldazzi, Fabio Kurita, Ryo Nakamura, Yukio Grosveld, Frank Philipsen, Sjaak Eich, Christina