Phase 1/2 AAV5-hRKp.RPGR (Botaretigene Sparoparvovec) Gene Therapy: Safety and Efficacy in RPGR-Associated X-Linked Retinitis Pigmentosa
Titel:
Phase 1/2 AAV5-hRKp.RPGR (Botaretigene Sparoparvovec) Gene Therapy: Safety and Efficacy in RPGR-Associated X-Linked Retinitis Pigmentosa
Auteur:
MICHAELIDES, MICHEL BESIRLI, CAGRI G. YANG, YESA DE GUIMARAES, THALES A.C. WONG, SUI CHIEN HUCKFELDT, RACHEL M. COMANDER, JASON I. SAHEL, JOSÉ-ALAIN SHAH, SYED MAHMOOD TEE, JAMES J.L. KUMARAN, NERUBAN GEORGIADIS, ANASTASIOS MINNICK, PANSY ZELDIN, ROBERT NAYLOR, STUART XU, JIALIN CLARK, MICHAEL ANGLADE, EDDY WONG, PEGGY FLECK, PENNY R. FUNG, ALBERT PELUSO, COLLEEN KALITZEOS, ANGELOS GEORGIOU, MICHALIS RIPAMONTI, CATERINA SMITH, ALEXANDER J. ALI, ROBIN R. FORBES, ALEXANDRIA BAINBRIDGE, JAMES