First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated Achromatopsia
Titel:
First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated Achromatopsia
Auteur:
Michaelides, Michel Hirji, Nashila Wong, Sui Chien Besirli, Cagri G. Zaman, Serena Kumaran, Neruban Georgiadis, Anastasios Smith, Alexander J. Ripamonti, Caterina Gottlob, Irene Robson, Anthony G. Thiadens, Alberta Henderson, Robert H. Fleck, Penny Anglade, Eddy Dong, Xiangwen Capuano, George Lu, Wentao Berry, Pamela Kane, Thomas Naylor, Stuart Georgiou, Michalis Kalitzeos, Angelos Ali, Robin R. Forbes, Alexandria Bainbridge, James