Safety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy
Titel:
Safety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy
Auteur:
VIGNAL-CLERMONT, CATHERINE YU-WAI-MAN, PATRICK NEWMAN, NANCY J. CARELLI, VALERIO MOSTER, MARK L. BIOUSSE, VALERIE SUBRAMANIAN, PREM S. WANG, AN-GUOR DONAHUE, SEAN P. LEROY, BART P. SADUN, ALFREDO A. KLOPSTOCK, THOMAS SERGOTT, ROBERT C. REBOLLEDA FERNANDEZ, GEMA CHWALISZ, BART K. BANIK, RUDRANI TAIEL, MAGALI ROUX, MICHEL SAHEL, JOSÉ-ALAIN