GUCY2D-Associated Leber Congenital Amaurosis: A Retrospective Natural History Study in Preparation for Trials of Novel Therapies
Titel:
GUCY2D-Associated Leber Congenital Amaurosis: A Retrospective Natural History Study in Preparation for Trials of Novel Therapies
Auteur:
Bouzia, Zaina Georgiou, Michalis Hull, Sarah Robson, Anthony G. Fujinami, Kaoru Rotsos, Tryfon Pontikos, Nikolas Arno, Gavin Webster, Andrew R. Hardcastle, Alison J. Fiorentino, Alessia Michaelides, Michel