Defining Outcomes for Clinical Trials of Leber Congenital Amaurosis Caused by GUCY2D Mutations
Titel:
Defining Outcomes for Clinical Trials of Leber Congenital Amaurosis Caused by GUCY2D Mutations
Auteur:
Jacobson, Samuel G. Cideciyan, Artur V. Sumaroka, Alexander Roman, Alejandro J. Charng, Jason Lu, Monica Choudhury, Shreyasi Schwartz, Sharon B. Heon, Elise Fishman, Gerald A. Boye, Shannon E.