Towards a clinical trial of lentivirus-mediated gene therapy for Fabry disease: In vitro patient cell mobilization and transduction outcomes
Titel:
Towards a clinical trial of lentivirus-mediated gene therapy for Fabry disease: In vitro patient cell mobilization and transduction outcomes
Auteur:
Rupar, Tony Khan, Aneal Au, Brian C. Tailor, Chet Rothe, Michael Bischof, Daniela Sirrs, Sandra Auray-Blais, Christiane Prokopishyn, Nicole O'Hoski, Pam Huang, Ju Paul, Gabi Benabid, Rym Viswanathan, Sowmya Morel, Chantal Raiman, Julian Schambach, Axel West, Michael Keating, Armand Cornetta, Ken Foley, Ronan Medin, Jeffrey A.