Patient- and family-oriented outcomes for inborn errors of metabolism: A scoping review
Title:
Patient- and family-oriented outcomes for inborn errors of metabolism: A scoping review
Author:
Khangura, Sara D. Chakraborty, Pranesh Coyle, Doug Karaceper, Maria D. Kronick, Jonathan B. Laberge, Anne-Marie Little, Julian Miller, Fiona Mitchell, John J. Prasad, Chitra Siriwardena, Komudi Sparkes, Rebecca Speechley, Kathy N. Stockler, Sylvia Tingley, Kylie Trakadis, Yannis Wilson, Brenda Wilson, Kumanan Zayed, Reem Potter, Beth K.