Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry
Titel:
Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry
Auteur:
Weinreb, Neal J Charrow, Joel Andersson, Hans C Kaplan, Paige Kolodny, Edwin H Mistry, Pramod Pastores, Gregory Rosenbloom, Barry E Scott, C.Ronald Wappner, Rebecca S Zimran, Ari