RNA Toxicity from the ALS/FTD C9ORF72 Expansion Is Mitigated by Antisense Intervention
Title:
RNA Toxicity from the ALS/FTD C9ORF72 Expansion Is Mitigated by Antisense Intervention
Author:
Donnelly, Christopher J. Zhang, Ping-Wu Pham, Jacqueline T. Haeusler, Aaron R. Mistry, Nipun A. Vidensky, Svetlana Daley, Elizabeth L. Poth, Erin M. Hoover, Benjamin Fines, Daniel M. Maragakis, Nicholas Tienari, Pentti J. Petrucelli, Leonard Traynor, Bryan J. Wang, Jiou Rigo, Frank Bennett, C. Frank Blackshaw, Seth Sattler, Rita Rothstein, Jeffrey D.