Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic
Titel:
Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic
Auteur:
Logan, Todd Simon, Matthew J. Rana, Anil Cherf, Gerald M. Srivastava, Ankita Davis, Sonnet S. Low, Ray Lieh Yoon Chiu, Chi-Lu Fang, Meng Huang, Fen Bhalla, Akhil Llapashtica, Ceyda Prorok, Rachel Pizzo, Michelle E. Calvert, Meredith E.K. Sun, Elizabeth W. Hsiao-Nakamoto, Jennifer Rajendra, Yashas Lexa, Katrina W. Srivastava, Devendra B. van Lengerich, Bettina Wang, Junhua Robles-Colmenares, Yaneth Kim, Do Jin Duque, Joseph Lenser, Melina Earr, Timothy K. Nguyen, Hoang Chau, Roni Tsogtbaatar, Buyankhishig Ravi, Ritesh Skuja, Lukas L. Solanoy, Hilda Rosen, Howard J. Boeve, Bradley F. Boxer, Adam L. Heuer, Hilary W. Dennis, Mark S. Kariolis, Mihalis S. Monroe, Kathryn M. Przybyla, Laralynne Sanchez, Pascal E. Meisner, Rene Diaz, Dolores Henne, Kirk R. Watts, Ryan J. Henry, Anastasia G. Gunasekaran, Kannan Astarita, Giuseppe Suh, Jung H. Lewcock, Joseph W. DeVos, Sarah L. Di Paolo, Gilbert