| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A methodological framework for drug development in rare diseases. The CRESim program: Epilogue and perspectives
|
Nony, Patrice
|
|
|
75 |
2 |
p. 149-156
|
artikel
|
| 2 |
An old drug for a rare disease: The example of celiprolol for vascular Ehlers-Danlos syndrome
|
Boutouyrie, Pierre
|
|
|
75 |
2 |
p. 175-181
|
artikel
|
| 3 |
Collaboration between academics, small pharmaceutical company and patient organizations in the development of a new formulation of cysteamine in nephropathic cystinosis: A successful story
|
Gaillard, Ségolène
|
|
|
75 |
2 |
p. 169-173
|
artikel
|
| 4 |
Drug repositioning for rare diseases: Knowledge-based success stories
|
Scherman, Daniel
|
|
|
75 |
2 |
p. 161-167
|
artikel
|
| 5 |
Drug repurposing in rare diseases: Myths and reality
|
Fetro, Christine
|
|
|
75 |
2 |
p. 157-160
|
artikel
|
| 6 |
Drugs and orphan diseases
|
Blin, Olivier
|
|
|
75 |
2 |
p. 131-132
|
artikel
|
| 7 |
Editorial board
|
|
|
|
75 |
2 |
p. i
|
artikel
|
| 8 |
Orphan drug clinical development
|
Blin, Olivier
|
|
|
75 |
2 |
p. 141-147
|
artikel
|
| 9 |
Orphan drug designation in Europe: A booster for the research and development of drugs in rare diseases
|
Micallef, Joëlle
|
|
|
75 |
2 |
p. 133-139
|
artikel
|
| 10 |
Patients’ organizations in rare diseases and involvement in drug information: Illustrations with LMC France, the French Association of Chronic Myeloid leukemia
|
Daban, Mina
|
|
|
75 |
2 |
p. 221-224
|
artikel
|
| 11 |
Pharmacovigilance and drug-induced rare diseases: Strengths of the French Network of Regional Pharmacovigilance Centres
|
Lacroix, Clémence
|
|
|
75 |
2 |
p. 207-213
|
artikel
|
| 12 |
The challenges of pharmacoepidemiology of orphan drugs in rare diseases
|
Lapeyre-Mestre, Maryse
|
|
|
75 |
2 |
p. 215-220
|
artikel
|
| 13 |
The key role of oncopharmacology in therapeutic management, from common to rare cancers: A literature review
|
Louveau, Baptiste
|
|
|
75 |
2 |
p. 183-193
|
artikel
|
| 14 |
Update on bradykinin-mediated angioedema in 2020
|
Lepelley, Marion
|
|
|
75 |
2 |
p. 195-205
|
artikel
|
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