Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study)
Title:
Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study)
Author:
Madruga-Garrido, Marcos Vázquez-Costa, Juan F. Medina-Cantillo, Julita Brañas, María Cattinari, María G. de Lemus, Mencía Díaz-Abós, Paola Sánchez-Menéndez, Victoria Terrancle, Ángeles Rebollo, Pablo Maurino, Jorge