Design and Rationale of the Global Phase 3 NEURO-TTRansform Study of Antisense Oligonucleotide AKCEA-TTR-LRx (ION-682884-CS3) in Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
Titel:
Design and Rationale of the Global Phase 3 NEURO-TTRansform Study of Antisense Oligonucleotide AKCEA-TTR-LRx (ION-682884-CS3) in Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
Auteur:
Coelho, Teresa Ando, Yukio Benson, Merrill D. Berk, John L. Waddington-Cruz, Márcia Dyck, Peter J. Gillmore, Julian D. Khella, Sami L. Litchy, William J. Obici, Laura Monteiro, Cecilia Tai, Li-Jung Viney, Nicholas J. Buchele, Gustavo Brambatti, Michela Jung, Shiangtung W. St. L. O’Dea, Louis Tsimikas, Sotirios Schneider, Eugene Geary, Richard S. Monia, Brett P. Gertz, Morie