Safety, Tolerability, and Pharmacokinetics of PTC124, a Nonaminoglycoside Nonsense Mutation Suppressor, Following Single- and Multiple-Dose Administration to Healthy Male and Female Adult Volunteers
Titel:
Safety, Tolerability, and Pharmacokinetics of PTC124, a Nonaminoglycoside Nonsense Mutation Suppressor, Following Single- and Multiple-Dose Administration to Healthy Male and Female Adult Volunteers
Auteur:
Hirawat, Samit Welch, Ellen M. Elfring, Gary L. Northcutt, Valerie J. Paushkin, Sergey Hwang, Seongwoo Leonard, Eileen M. Almstead, Neil G. Ju, William Peltz, Stuart W. Miller, Langdon L.