Immunogenicity to cerliponase alfa intracerebroventricular enzyme replacement therapy for CLN2 disease: Results from a Phase 1/2 study
Titel:
Immunogenicity to cerliponase alfa intracerebroventricular enzyme replacement therapy for CLN2 disease: Results from a Phase 1/2 study
Auteur:
Cherukuri, Anu Cahan, Heather de Hart, Greg Van Tuyl, Andrea Slasor, Peter Bray, Laurie Henshaw, Joshua Ajayi, Temitayo Jacoby, Dave O'Neill, Charles A. Schweighardt, Becky