The first reported generation of several induced pluripotent stem cell lines from homozygous and heterozygous Huntington's disease patients demonstrates mutation related enhanced lysosomal activity
Titel:
The first reported generation of several induced pluripotent stem cell lines from homozygous and heterozygous Huntington's disease patients demonstrates mutation related enhanced lysosomal activity
Auteur:
Camnasio, Stefano Carri, Alessia Delli Lombardo, Angelo Grad, Iwona Mariotti, Caterina Castucci, Alessia Rozell, Björn Riso, Pietro Lo Castiglioni, Valentina Zuccato, Chiara Rochon, Christelle Takashima, Yasuhiro Diaferia, Giuseppe Biunno, Ida Gellera, Cinzia Jaconi, Marisa Smith, Austin Hovatta, Outi Naldini, Luigi Di Donato, Stefano Feki, Anis Cattaneo, Elena