Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trial
Title:
Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trial
Author:
Diaz-Manera, Jordi Kishnani, Priya S Kushlaf, Hani Ladha, Shafeeq Mozaffar, Tahseen Straub, Volker Toscano, Antonio van der Ploeg, Ans T Berger, Kenneth I Clemens, Paula R Chien, Yin-Hsiu Day, John W Illarioshkin, Sergey Roberts, Mark Attarian, Shahram Borges, Joao Lindolfo Bouhour, Francoise Choi, Young Chul Erdem-Ozdamar, Sevim Goker-Alpan, Ozlem Kostera-Pruszczyk, Anna Haack, Kristina An Hug, Christopher Huynh-Ba, Olivier Johnson, Judith Thibault, Nathan Zhou, Tianyue Dimachkie, Mazen M Schoser, Benedikt