Gain of Toxicity from ALS/FTD-Linked Repeat Expansions in C9ORF72 Is Alleviated by Antisense Oligonucleotides Targeting GGGGCC-Containing RNAs
Title:
Gain of Toxicity from ALS/FTD-Linked Repeat Expansions in C9ORF72 Is Alleviated by Antisense Oligonucleotides Targeting GGGGCC-Containing RNAs
Author:
Jiang, Jie Zhu, Qiang Gendron, Tania F. Saberi, Shahram McAlonis-Downes, Melissa Seelman, Amanda Stauffer, Jennifer E. Jafar-nejad, Paymaan Drenner, Kevin Schulte, Derek Chun, Seung Sun, Shuying Ling, Shuo-Chien Myers, Brian Engelhardt, Jeffery Katz, Melanie Baughn, Michael Platoshyn, Oleksandr Marsala, Martin Watt, Andy Heyser, Charles J. Ard, M. Colin De Muynck, Louis Daughrity, Lillian M. Swing, Deborah A. Tessarollo, Lino Jung, Chris J. Delpoux, Arnaud Utzschneider, Daniel T. Hedrick, Stephen M. de Jong, Pieter J. Edbauer, Dieter Van Damme, Philip Petrucelli, Leonard Shaw, Christopher E. Bennett, C. Frank Da Cruz, Sandrine Ravits, John Rigo, Frank Cleveland, Don W. Lagier-Tourenne, Clotilde