RNA Toxicity from the ALS/FTD C9ORF72 Expansion Is Mitigated by Antisense Intervention
Titel:
RNA Toxicity from the ALS/FTD C9ORF72 Expansion Is Mitigated by Antisense Intervention
Auteur:
Donnelly, Christopher J. Zhang, Ping-Wu Pham, Jacqueline T. Haeusler, Aaron R. Mistry, Nipun A. Vidensky, Svetlana Daley, Elizabeth L. Poth, Erin M. Hoover, Benjamin Fines, Daniel M. Maragakis, Nicholas Tienari, Pentti J. Petrucelli, Leonard Traynor, Bryan J. Wang, Jiou Rigo, Frank Bennett, C. Frank Blackshaw, Seth Sattler, Rita Rothstein, Jeffrey D.